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Clinical trials test new treatments โ€” sometimes the newest options available for a disease. Find trials that are recruiting now, near you. Open one to see its eligibility rules as simple questions to go through with your doctor.

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30 recruiting trials

for Familial Hypercholesterolemias

Study of Zodasiran in Adolescent Participants With Homozygous Familial Hypercholesterolemia NCT07473843Phase 33 sites๐Ÿ“ St Louis๐Ÿ“ Viborg๐Ÿ“ Warsaw Arrowhead Pharmaceuticals ยท Tests: Zodasiran A Study to Evaluate the SYH2053 Injection in Patients With Heterozygous Familial Hypercholesterolemia (HeFH) NCT07465263Phase 31 site๐Ÿ“ Beijing CSPC Zhongnuo Pharmaceutical (Shijiazhuang) Co., Ltd. ยท Tests: SYH2053 Injection, Placebo Injection A Study to Evaluate the Safety, Efficacy of SYH2053 as Monotherapy in Chinese Participants With Non-familial Hypercholesterolemia or Mixed Hyperlipidemia NCT07421297Phase 32 sites๐Ÿ“ Beijing๐Ÿ“ Beijing CSPC Zhongnuo Pharmaceutical (Shijiazhuang) Co., Ltd. ยท Tests: SYH2053 injection, SYH2053 injection placebo Child-Parent Familial Hypercholesterolemia Screening NCT04529967n/a6 sites๐Ÿ“ Hefei๐Ÿ“ Qidong๐Ÿ“ Shanghai Children's Hospital of Fudan University ยท Tests: no interventions Familial Hypercholesterolemia Canada / Hypercholesterolemie Familiale Canada NCT02009345n/a1 site๐Ÿ“ Montreal McGill University Health Centre/Research Institute of the Mโ€ฆ Early Detection of Familial Hypercholesterolemia in Children NCT04370899n/a2 sites๐Ÿ“ Reus๐Ÿ“ Reus Institut Investigacio Sanitaria Pere Virgili ยท Tests: lifestyle assessment Study to Evaluate Safety, Tolerability and Efficacy of Inclisiran in Children With Homozygous Familial Hypercholesterolemia NCT06597006Phase 319 sites๐Ÿ“ San Francisco๐Ÿ“ Washington D.C.๐Ÿ“ St Louis Novartis Pharmaceuticals ยท Tests: Inclisiran, Placebo Computerized Decision Support for Identification and Management of Familial Hypercholesterolemia NCT06743659NA1 site๐Ÿ“ Boston Brigham and Women's Hospital ยท Tests: Alert-based computerized decision support Russian Familial Hypercholesterolemia Registry NCT02208869n/a5 sites๐Ÿ“ Chelyabinsk๐Ÿ“ Moscow๐Ÿ“ Novosibirsk Russian Cardiology Research and Production Center The Spanish Familial Hypercholesterolaemia Cohort Study NCT02693548n/a1 site๐Ÿ“ Madrid Fundaciรณn Hipercolesterolemia Familiar A Real-World Study of Long-Term Adherence and Persistence to Inclisiran, Evolocumab, and Alirocumab NCT07543731n/a1 site๐Ÿ“ Basel Novartis Pharmaceuticals Phase 3 Clinical Study Evaluating Efficacy, Safety, and Tolerability of Obicetrapib Vs Bempedoic Acid to Treat Dyslipidemia in Adults With Primary Non-familial Hypercholesterolemia or Mixed Dyslipidemia at High to Very High Cardiovascular Risk, During a Treatment Period of Approximately 84 Days NCT07614958Phase 31 site๐Ÿ“ Stockton-on-Tees A. Menarini International Licensing S.A. ยท Tests: Obicetrapib 10 mg/Bempedoic Acid Placebo, Bempedoic Acid 180mg/Placebo Obicetrapib Long-term Safety and Tolerability of Inclisiran in Participants With HeFH or HoFH Who Have Completed the Pediatric ORION-16, ORION-13, ORION-20, or ORION-19 Studies NCT05682378Phase 352 sites๐Ÿ“ Boca Raton๐Ÿ“ New York๐Ÿ“ Cincinnati Novartis Pharmaceuticals ยท Tests: Inclisiran A Study of Enlicitide Decanoate (MK-0616, an Oral PCSK9 Inhibitor) in Children and Adolescents With Heterozygous Familial Hypercholesterolemia (MK-0616-029) NCT07058077Phase 2, Phase 347 sites๐Ÿ“ Wilmington๐Ÿ“ Washington D.C.๐Ÿ“ Boca Raton Merck Sharp & Dohme LLC ยท Tests: Enlicitide Decanoate, Placebo Study to Evaluate Efficacy and Safety of Inclisiran in Children With Heterozygous Familial Hypercholesterolemia NCT06597019Phase 366 sites๐Ÿ“ San Francisco๐Ÿ“ San Francisco๐Ÿ“ Washington D.C. Novartis Pharmaceuticals ยท Tests: Inclisiran, Placebo NGGT006 Gene Therapy for Homozygous Familial Hypercholesterolemia NCT06125847EARLY Phase 11 site๐Ÿ“ Xi'an First Affiliated Hospital Xi'an Jiaotong University ยท Tests: NGGT006 Study of the Determinants of Coronary Atherosclerosis in Familial Hypercholesterolemia (ATHERO-FH Study) NCT06960902NA9 sites๐Ÿ“ Dijon๐Ÿ“ Lille๐Ÿ“ Lyon Nantes University Hospital ยท Tests: Coronary CT scan with CAC score measurement The ORIGIN-FH Study NCT07470723NA1 site๐Ÿ“ Madison University of Wisconsin, Madison ยท Tests: Screening for FH Atlantic Lipid Lowering Treatment Optimization Program NCT06439654NA2 sites๐Ÿ“ Clark๐Ÿ“ Springfield Atlantic Health System ยท Tests: Supportive care Integrating Whole Genome Sequencing and Digital Twins Into the Management of Hypercholesterolemia in Emiratis NCT06535542NA1 site๐Ÿ“ Abu Dhabi Abu Dhabi Health Services Company ยท Tests: Whole Genome Sequencing Phase 1b Study of VERVE-201 in Patients With Refractory Hyperlipidemia NCT06451770Phase 118 sites๐Ÿ“ Garden Grove๐Ÿ“ Clearwater๐Ÿ“ Miami Lakes Verve Therapeutics, Inc. ยท Tests: VERVE-201 A Dose-exploration Study of EDP167 in HoFH NCT07489209Phase 21 site๐Ÿ“ Beijing Eddingpharm (Zhuhai) Co., Ltd. ยท Tests: EDP167 EAS Familial Hypercholesterolaemia Studies Collaboration NCT04272697n/a1 site๐Ÿ“ London Imperial College London Screening for Familial Hypercholesterolemia in Children NCT06555120NA1 site๐Ÿ“ Amiens Centre Hospitalier Universitaire, Amiens ยท Tests: blood sample Multicomponent Intervention Study- Blood Donors With High Cholesterol NCT05693701NA1 site๐Ÿ“ Dallas University of Texas Southwestern Medical Center ยท Tests: Implementation Strategy Bundle, Usual care notification The Rogosin Institute Homozygous Familial Hypercholesterolemia Repository NCT01109368n/a1 site๐Ÿ“ New York The Rogosin Institute Familial Hypercholesterolemia Interpretive Comment - Nudging to Detection. NCT05614219NA2 sites๐Ÿ“ Odense๐Ÿ“ Odense C Odense University Hospital ยท Tests: Biochemistry interpretive comment on elevated LDL-C levels National Network for Cardiovascular Genomics: Advancing Cardiovascular Healthcare for Hereditary Diseases in Brazil's Unified Health System Through a Multicenter Registry NCT06546137n/a27 sites๐Ÿ“ Rio Branco๐Ÿ“ Maceiรณ๐Ÿ“ Macapรก Hospital do Coracao ยท Tests: whole genome sequencing Phase II Clinical Trial to Evaluate the Efficacy and Safety of SYH2070 Injection in Participants With Homozygous Familial Hypercholesterolemia NCT07591298Phase 21 site๐Ÿ“ Changsha CSPC Zhongnuo Pharmaceutical (Shijiazhuang) Co., Ltd. ยท Tests: SYH2070 injection dose1, SYH2070 injection dose2 High Intensity Interval Training in the Treatment of Familial Hypercholesterolemia (UPPA-FH) NCT06833944NA1 site๐Ÿ“ Granada Fundaciรณn Pรบblica Andaluza para la Investigaciรณn Biomรฉdica โ€ฆ ยท Tests: HIIT intervention program, MICT intervention program
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